designated intractable/rare disease
disease/syndrome specified according to Japanese law
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Instances
104
Influences rating
Influences rating
Stevens–Johnson syndrome
Rheumatoid arthritis
Ulcerative colitis
Parkinson's disease
Multiple sclerosis
Autoimmune hemolytic anemia
Tetralogy of Fallot
Familial hypercholesterolemia
Tangier disease
Crohn's disease